This week, a remarkable scientific breakthrough was achieved with the first-ever application of a personalized in vivo gene editing treatment in a baby. Researchers developed a therapy targeting a rare mutation in the *CPS1* gene, showing significant improvement after three doses and opening new possibilities in precision medicine.
Can vision loss be reversed?
🧬This Breakthrough Study Reveals New Hope👁️ A rare cause of congenital (present at birth) vision loss is severe retinal dystrophy associated with the gene AIPL1. Until recently, this condition, like many other rare diseases, had no available treatment. However, a recent study published in The Lancet has demonstrated the transformative potential of gene therapy to change this … Sigue leyendo Can vision loss be reversed?
Dra Adriana Perez-Grovas Saltijeral 
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